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Sionna Therapeutics, Inc.

Pipeline8 assets

  • SION-719SION-719 / NBD1 (Nucleotide Binding Domain 1 of CFTR) / Small Molecule / Respiratory / Genetic Diseases
    Cystic FibrosisPhase 2aActive
  • SION-451SION-451 / NBD1 (Nucleotide Binding Domain 1 of CFTR) / Small Molecule / Respiratory / Genetic Diseases
    Cystic FibrosisPhase 1Active
  • SION-638SION-638 / NBD1 (Nucleotide Binding Domain 1 of CFTR) / Small Molecule / Respiratory / Genetic Diseases
    Cystic FibrosisPhase 1Active
  • SION-109SION-109 / ICL4 (Intracellular Loop 4 of CFTR) / Small Molecule / Respiratory / Genetic Diseases
    Cystic FibrosisPhase 1Active
  • GalicaftorABBV-2222 / TMD1-directed CFTR corrector / Small Molecule / Respiratory / Genetic Diseases
    Cystic FibrosisPhase 2Active
  • NavocaftorABBV-3067 / CFTR potentiator / Small Molecule / Respiratory / Genetic Diseases
    Cystic FibrosisPhase 2Active
  • ABBV-2851ABBV-2851 / TMD1-directed CFTR corrector / Small Molecule / Respiratory / Genetic Diseases
    Cystic FibrosisPhase 1Active
  • SION-676SION-676 / TMD1-directed CFTR corrector / Small Molecule / Respiratory / Genetic Diseases
    Cystic FibrosisPreclinicalActive

Latest news9 items

All news

Sionna Therapeutics Reports First Quarter 2026 Financial Results

Enrollment completed in the PreciSION CF Phase 2a proof-of-concept trial evaluating NBD1 stabilizer SION-719 as an add-on to standard of care in participants with cystic fibrosis; topline data on track for the summer of 2026 Ongoing Phase 1 trial evaluating NBD1 stabilizer SION-451 in proprietary

Enrollment • Phase 2Enrollment completion Wed, Apr 1, 2026

Sionna Therapeutics Completes Enrollment in PreciSION CF Phase 2a Trial Evaluating NBD1 Stabilizer, SION-719, Added to Standard of Care in Participants with Cystic Fibrosis

Topline data is on track for anticipated readout in the summer of 2026 WALTHAM, Mass., April 27, 2026 (GLOBE NEWSWIRE) -- Sionna Therapeutics, Inc. (Nasdaq: SION), a clinical-stage biopharmaceutical company on a mission to revolutionize the current treatment paradigm for cystic fibrosis (CF), today

Enrollment • Phase 2
Sionna Therapeutics, Inc. • Endpoint Arena